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Catalog Models

PD1 Humanized Mouse Models

PD1 humanized mice enable preclinical testing of anti human PD1 therapeutic antibodies including pembrolizumab and nivolumab in immunocompetent mouse systems.

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Why Humanize PD1

Species Specificity of Therapeutic Antibodies

Anti PD1 therapeutic antibodies are engineered specifically for human PD1:

  • Antibody epitopes designed against human PD1 sequence
  • Limited or no binding to mouse PD1 ortholog
  • Cannot evaluate efficacy in wildtype mice
  • Surrogate antibodies against mouse PD1 may not predict human responses

Humanized PD1 mice express the human target, enabling direct testing of clinical antibody candidates.

Maintaining Immunocompetent System

PD1 humanization preserves the mouse immune system:

  • Functional T cells expressing human PD1
  • Intact tumor microenvironment interactions
  • Normal immune cell development and function
  • Physiological PD1/PDL1 axis signaling

Unlike xenograft models in immunodeficient mice, humanized checkpoint models enable immunotherapy studies in animals with functional adaptive immunity.

Translational Relevance

Humanized models improve translation to clinical outcomes:

  • Test the actual clinical candidate, not a surrogate
  • Evaluate on target effects with human protein engagement
  • Develop and validate human specific biomarkers
  • Support regulatory submissions with relevant efficacy data

Humanization Strategies

Extracellular Domain Humanization

The most common approach replaces the mouse PD1 extracellular domain with human sequence while retaining mouse intracellular signaling domains:

Human extracellular domain provides antibody binding epitopes
Mouse transmembrane and intracellular domains preserved
Normal signaling through mouse downstream pathways
Maintained compatibility with mouse immune system

This strategy is optimal for therapeutic antibody testing where the goal is to evaluate antibody binding and blocking activity.

Complete Gene Humanization

Full replacement of mouse Pdcd1 with human PDCD1:

Complete human PD1 protein sequence
Human specific signaling characteristics
Study human PD1 biology comprehensively
May require consideration of species specific interactions

Conditional Humanization

Conditional approaches enable controlled humanization:

Tissue specific humanization using Cre lox
Inducible humanization for temporal control
Compare humanized and mouse PD1 in same animal

Applications

Anti PD1 Antibody Efficacy Testing

Primary application for PD1 humanized mice:

  • Test pembrolizumab, nivolumab, and other clinical antibodies
  • Evaluate novel anti PD1 candidates
  • Compare antibody potency and characteristics
  • Assess Fc effector function contributions

Combination Immunotherapy

PD1 humanized mice support combination studies:

  • Anti PD1 plus chemotherapy
  • Anti PD1 plus radiation
  • Anti PD1 plus targeted therapy
  • Anti PD1 plus other checkpoint inhibitors (dual humanized models)

Tumor Model Compatibility

PD1 humanized mice on C57BL/6 background are compatible with syngeneic tumor models. BALB/c background humanized models enable use of CT26, 4T1, and other BALB/c compatible tumor lines.

Biomarker Development

Humanized models support translational biomarker work:

  • Human PD1 detection with clinical grade antibodies
  • Pharmacodynamic biomarker validation
  • Receptor occupancy assessment
  • Immune activation markers

Tumor Model Compatibility

Tumor ModelTumor TypePD1/PDL1 Response
MC38Colon carcinomaResponsive
B16MelanomaVariable
LLCLung carcinomaVariable
E0771Breast carcinomaResponsive

Combination with Other Humanized Checkpoints

PD1 humanization can be combined with other checkpoint humanizations. Dual humanized models enable evaluation of combination checkpoint inhibitor regimens using clinical antibodies against both targets.

Combination Models

CombinationApplications
PD1 + CTLA4Ipilimumab + nivolumab combinations
PD1 + LAG3Next generation checkpoint combinations
PD1 + TIM3Emerging combination strategies
PD1 + TIGITNovel checkpoint combinations

For complex combination studies, multiple checkpoint humanizations can be combined through breeding or sequential targeting. Our scientific team advises on efficient strategies for generating multi humanized models.

Technical Considerations

Strain Background

Choose strain background based on tumor model compatibility:

  • C57BL/6: Compatible with MC38, B16, LLC, E0771
  • BALB/c: Compatible with CT26, 4T1, EMT6

Our scientific team advises on optimal strain background for your research program.

Functional Validation

Validate humanized PD1 function in your experimental system:

  • Confirm human PD1 surface expression on T cells
  • Verify therapeutic antibody binding
  • Test functional checkpoint blockade
  • Compare to wildtype controls

Selected Publications

Humanized checkpoint models generated by ingenious targeting laboratory have supported immuno oncology research:

Mlynarczyk C et al. 2023. BTG1 mutation yields supercompetitive B cells primed for malignant transformation. Science 379(6629): eabj0412.

Chakrabarti S et al. 2024. Touch sensation requires the mechanically gated ion channel ELKIN1. Science 383(6686): 992 to 998.

Clausen BE et al. 1999. Conditional gene targeting in macrophages and granulocytes using LysMcre mice. Transgenic Research 8(4): 265 to 277.

What Researchers Say

iTL produced a new conditional mouse model for us and the quality of service was exceptional. The team is extremely knowledgeable and the work was completed at the highest possible standards. My project manager was excellent and always happy to answer technical questions and keep me up to date with progress and potential problems. I would recommend iTL highly and will use them again in the future if I need to generate a new mouse line.

Albert Basson, PhD

King's College London

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✦ New for 2026

Breeding Scheme Architect

Plan complex multi-allele breeding strategies, calculate expected genotype ratios, and estimate time to experimental cohorts—all before starting your project.

Visualize multi-generation breeding paths
Calculate Mendelian ratios automatically
Estimate timeline to study-ready cohorts

Free Research Tool

No account required

Allele 1Gene-flox (conditional)
Allele 2Cre-driver (tissue-specific)
TargetHomozygous knockout

→ 3 generations to target genotype

Start Your PD1 Humanization Project

Our scientific consultants are ready to discuss your PD1 humanization requirements and recommend the optimal strategy for your immuno oncology program. Initial consultation is provided at no charge and includes humanization approach recommendations, strain background guidance, and timeline estimates.

Frequently Asked Questions

Full humanization replaces the entire mouse PD1 gene with human PD1 sequence. ECD-only humanization replaces only the extracellular domain while retaining mouse transmembrane and cytoplasmic domains. Full humanization is preferred for antibody testing; ECD-only may preserve some mouse signaling functions.

Yes. PD1 humanization can be combined with PDL1, CTLA4, LAG3, TIM3, or other checkpoint humanizations to create double, triple, or multi-checkpoint models. Common combinations include PD1+CTLA4 and PD1+LAG3 for combination checkpoint blockade studies.

Yes. PD1 humanized mice on C57BL/6 background are compatible with syngeneic tumor models (MC38, B16, LLC, E0771) to create systems where both tumor and immune compartments express human targets. This enables evaluation of checkpoint blockade in immunocompetent animals with intact tumor immunity.

Lab Signals

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